Understanding the Causes of Rett Syndrome

Certain key things are known about what causes Rett, which is a huge advantage in terms of trying to find treatments and a cure. We know that: It is a single gene disorder. It has been widely demonstrated to be reversible when the missing protein is replaced

Approaches to Research

There are several different approaches in terms of research: putting the protein back: this approach aims to recreate the successful reversal experiments on mice, from 2007, which showed that putting the MeCP2┬áprotein back reverses the symptoms of Rett.   improving symptoms: many of the symptoms of Rett could